Publications
- Combinatorial base editing couples disease correction with lineage amplification in hematopoietic stem and progenitor cells.
2026 |
PubMed
- In utero genetic therapy: Treatment of early onset neurological disorders before they start.
2025 |PubMed
- Single nuclei and spatial profiling of sacrococcygeal teratomas reveals cellular composition and X inactivation heterogeneity.
2026 |PubMed
- GFP-on mouse model for interrogation of in vivo gene editing.
2025 |PubMed
- Single-cell spatiotemporal dissection of the human maternal-fetal interface.
2026 |PubMed
- Evidence for Maternal Autoantibodies in the Pathogenesis of Preterm Birth.
2025 |PubMed
- In Utero Hematopoietic Cell Transplantation in Fetuses with Alpha Thalassemia Major: A Phase 1 Clinical Trial.
2026 |PubMed
- Integrated single-nuclei and spatial transcriptomic profiling of human sacrococcygeal teratomas reveals heterogeneity in cellular composition and X-chromosome inactivation.
2025 |PubMed
- Attitudes Toward Prenatal Interventions in the Fanconi Anemia Community.
2026 |PubMed
- Lentiviral vectors for hematopoietic stem cell gene therapy restore α-globin expression in α-thalassemia red blood cells.
2025 |PubMed